gene therapy
Cellular code repair
Gene therapy is medical treatment that modifies a person's genes to treat or prevent disease.
It may involve replacing a faulty gene, inactivating a malfunctioning one, or introducing new genetic material.
The approach holds promise for inherited disorders, certain cancers, and viral infections: Gene therapy offers hope for patients with cystic fibrosis.
Gene-editing molecular machinery
- Cas9DNA-cutting enzyme
- adenovirusDNA virus infecting airways
- lentivirusLong-incubation retrovirus type
- antisenseGene-silencing nucleic acid
in vivo · transfection · transduction · delivery system · microinjection
Gene-bearing nuclear structures
- DNAHereditary code molecule
- nucleotideGenetic code subunit
- mutationPermanent DNA alteration
- allelesVariant forms of genes
heredity · base pairs · double helix · transcription · translation · replication · recombination · vectors
Care for an ailment
- cureTreatment that heals
- clinical trialsControlled health research experiments
- patientsThose receiving medical treatment
- remissionTemporary disease absence
FDA approval · rare diseases · inherited disorders · cancer treatment · immunotherapy · muscular dystrophy · cystic fibrosis · hemophilia
Moral philosophy for medicine
- consentVoluntary agreement given
- regulationOfficial rules governing conduct
- eugenicsControlled human reproduction theory
- designer babiesGenetically customized offspring
accessibility · inequality · oversight · moratorium · human dignity · informed consent · risk assessment · long-term effects
Engineering using living systems
- clinical trialsControlled health research experiments
- preclinicalBefore human trials
- biomedical researchScientific study of health
- laboratoryFacility for scientific investigation
peer review · funding · pharmaceutical · translational · FDA · regulatory approval · proof of concept · investigational
CRISPR
Gene-editing molecular machinery
- Cas9DNA-cutting enzyme
- adenovirusDNA virus infecting airways
- lentivirusLong-incubation retrovirus type
antisense · in vivo · transfection · transduction · delivery system · microinjection
chromosomes
Gene-bearing nuclear structures
- DNAHereditary code molecule
- nucleotideGenetic code subunit
- mutationPermanent DNA alteration
alleles · heredity · base pairs · double helix · transcription · translation · replication · recombination · vectors · plasmids
treatment
Care for an ailment
- cureTreatment that heals
- clinical trialsControlled health research experiments
- patientsThose receiving medical treatment
remission · FDA approval · rare diseases · inherited disorders · cancer treatment · immunotherapy · muscular dystrophy · cystic fibrosis · hemophilia · sickle cell
bioethics
Moral philosophy for medicine
- consentVoluntary agreement given
- regulationOfficial rules governing conduct
- eugenicsControlled human reproduction theory
designer babies · accessibility · inequality · oversight · moratorium · human dignity · informed consent · risk assessment · long-term effects · unintended consequences
biotechnology
Engineering using living systems
- clinical trialsControlled health research experiments
- preclinicalBefore human trials
- biomedical researchScientific study of health
laboratory · peer review · funding · pharmaceutical · translational · FDA · regulatory approval · proof of concept · investigational · endpoints
- cancer treatmentchemotherapy, immunotherapy, surgery, radiotherapy, cancer surgery
- Gene Therapytransgene, transgenes, CRISPR, antisense, plasmids
- biomedical researchanimal model, animal testing, drug testing, clinical trial, xenograft
- cell engineeringcell culture, transfection, transduction, CRISPR, cloning
- nanomedicinenanomedicine, nanoparticles, liposomes, mRNA vaccines, Moderna vaccine
- Rare Disease Drugs
gene therapypalliative care
Relief-focused medicine for illness
drug therapy · chemotherapy · pharmacotherapy · supportive care · surgery
gene therapynatural healing
Body's innate restorative processes
letting nature take its course · traditional medicine · herbal medicine · holistic medicine · folk remedies
gene therapygenetic enhancement
Modifying hereditary material deliberately
eugenics · designer babies · human enhancement · transhumanism
therapy, therapist, genes, genetic, gene, genealogy, therapeutic, genetics, genome